Inhibition of Dcps

The disclosure relates to methods and compositions (e.g., compounds and pharmaceutical compositions thereof) useful for increasing expression of SMN in a cell (e.g., in vitro or in vivo). As a deficiency in SMN can result in the development of an SMA condition in a subject, the methods and compositions described herein can also be used to, e.g., treat, or prevent, an SMA condition in a subject.

Attached files:


Patents:
WO 2,009,120,700

Inventor(s): JARECKI JILL [US]; SINGH JASBIR [US]; GURNEY MARK [US]; POLLOK BRIAN [US]; MICHAUD GREGORY [US]; LIU SHIN-WU [US]; KILEDJIAN MEG

Type of Offer: Licensing



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